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The CuRe trial is now enrolling up to 35 patients in its Phase 1/2a study. Children will be followed through age 6 to evaluate long-term safety and early signs of improved movement, bladder and bowel function.

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与此同时,和誉医药等本土药企也在精准靶向赛道加速布局,新一代疗法的比拼已然拉开帷幕。从FIC到精准治疗的BIC,谁能登顶,定义ACH下一代治疗标准?

Reporting by Chance Townsend, Caitlin Welsh, Sam Haysom, Amanda Yeo, Shannon Connellan, Cecily Mauran, Mike Pearl, and Adam Rosenberg contributed to this article.

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